The lone volunteer in a gene-editing study targeting a rare form of Duchenne muscular dystrophy likely died after having a reaction to the virus that delivered the therapy in his body, researchers ...
Epicrispr Reports Early Clinical Activity and Favorable Safety Profile in First-in-Human Epigenetic Editing Study for FSHD ...
Please provide your email address to receive an email when new articles are posted on . A single-dose CRISPR gene-editing infusion lowered blood PCSK9 in three patients with HeFH and advanced CAD. One ...
The CRISPR-based genome editing toolbox is packed with powerful refinements. The latest of these, prime editing (PE), was first reported in Nature in 2019 by David Liu’s group. Using a prime editing ...
A condition called CD3 delta SCID is caused by a mutation in the CD3D gene, which prevents the production of the CD3 delta protein that is needed for the normal development of T cells from blood stem ...
This is an archived article and the information in the article may be outdated. Please look at the time stamp on the story to see when it was last updated. The lone volunteer in a gene-editing study ...
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